Our Blog
Rare Perspectives
Insights and information on our approach to collaborating with rare disease communities, supporting our teammates at Ultragenyx, and developing new therapies for rare disease.
Featured Post
GUEST POST: My Journey from Hope to a Potential First Therapy for Angelman Syndrome
GeneTx founder reflects on path from parent to drug developer and partnership with Ultragenyx
Blog Categories
- Advocacy
- All Categories
- Citizenship
- Culture
- Research
