Rare perspective blog
Insights on our approach to collaborating with the rare disease community, supporting our teammates at Ultragenyx, and developing new therapies for rare diseases.
Latest posts
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September 21, 2023 Advocacy Achieving the Life-saving Potential of Newborn Screening After 60 Years of Newborn Screening, Political Leadership is Needed to Ensure Rare Disease Diagnosis Keeps Pace with Science Read more >
- July 10, 2023 Advocacy Guest Post: living with osteogenesis imperfecta (OI) Learning to trust yourself and take calculated risks Read more >
- July 3, 2023 Research VIDEO: a turning point for gene therapy production Ultragenyx begins a new era in gene therapy manufacturing Read more >