Developing innovative therapies for those living with serious rare and ultrarare genetic diseases

Our approach has led to the delivery of multiple first-ever rare disease treatments at a faster speed than the industry average.

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CRYSVITA®

CRYSVITA® (burosumab-twza) logo

Patients and healthcare providers, learn more at CRYSVITA.com

Report a side effect

You may report side effects to the FDA at 1-800-FDA-1088 or www.fda.gov/medwatch

You may also report side effects to Kyowa Kirin at 1-844-768-3544.

MEPSEVII®

MEPSEVII® (vestronidase alfa-vjbk) logo

Patients and healthcare providers, learn more at MEPSEVII.com

Read the U.S. Prescribing Information for MEPSEVII

UltraCare: Our program to help facilitate patient access to our medicines. Learn more at UltraCareSupport.com

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Latest news

Get the latest information related to our company, our pipeline, and our medicines.

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Pipeline Med Card

Pipeline

Discover our portfolio of therapies in development.

View our pipeline