Grants and

Ultragenyx is committed to supporting initiatives that provide impactful resources for the rare disease community, healthcare education, STEAM education, and local community organizations.

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Independent medical education

Ultragenyx offers educational grants for accredited and non-accredited clinical, technical, and scientific programs or continuing medical education activities focused on rare diseases for healthcare providers.

In certain clinical areas, a request for proposal (RFP) will be posted to this site for independent medical education. Please check back for more information or reach out to Ultragenyx Grants Program at [email protected].

We are currently considering independent medical education in the following areas:

  • X-linked hypophosphatemia (XLH)
  • Tumor-induced osteomalacia (TIO)
  • Mucopolysaccharidosis type VII (MPSVII)
  • Long-chain fatty acid oxidation disorders (LC-FAOD)
  • Homozygous familial hypercholesterolemia (HoFH)—ex-U.S. only
  • General gene therapy education

Learn more about independent medical education

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Health-related grant funding

Sponsorships and grants for nonprofit patient organizations and for-profit health institutions in support of:

  • Patient advocacy—focused initiatives
    • Patient education
    • Patient, family, and caregiver meetings and events
    • Patient community events
  • Scientific meetings (non-accredited)
  • Disease awareness campaigns
  • Research programs
  • Non-interventional studies
  • Medical publications (Europe and Latin America only)
  • Fellowships
  • Sponsorships

We are currently considering health-related grant funding in the following areas:

  • Bone endocrine: X-linked hypophosphatemia, tumor-induced osteomalacia, osteogenesis imperfecta
  • Metabolics: mucopolysaccharidosis type VII, long-chain fatty acid oxidation disorders, glycogen storage disease (GSD) type Ia and type III, ornithine transcarbamylase deficiency, Wilson disease, creatine transporter deficiency, homozygous familial hypercholesterolemia (HoFH)
  • Central nervous system and neurology: Angelman syndrome, Duchenne muscular dystrophy, CDKL5

Learn more about health-related grants

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Charitable donations

Our global corporate philanthropy program supports public health and wellness, educational, and humanitarian initiatives directed towards the rare disease community and other local or at-risk communities. Specifically, we focus on:

  • Science, technology, engineering, the arts, and mathematics (STEAM) education, including diversity, equity, and inclusion (DEI) initiatives, scholarships, and science events or programs
  • Rare disease community support, including patient or sibling programs, respite care or support programs for care partners, and awareness initiatives
  • Equitable healthcare, including public health initiatives, access to services, and wellness for underserved communities with the aim to reduce healthcare disparities
  • Emergency relief aid, including providing immediate assistance during humanitarian crises, particularly in the areas of public health and medical services

Learn more about charitable donations

We require all funding applications be submitted through our Grants Portal

Requests for grant funding should be submitted 30 days prior to the date you require a decision or a minimum of 60 days prior to your program start date, though longer periods are encouraged. All applications are formally and thoughtfully reviewed by a dedicated committee(s) of representatives. Once submitted, you will be notified by email with our decision.

Eligibility to Apply (optional tool to help you determine the correct type of grant request)

For more information about the Ultragenyx Grants Program, please contact [email protected].

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