Our Pipeline
Diverse clinical and preclinical pipeline
We are advancing clinical development programs across multiple rare disease therapeutic areas and drug modalities. We also have a broad translational research department with more than 15 different programs and the goal to advance one new program into clinical trials every one to two years.
BIOLOGIC
DESCRIPTION
PRE-CLINICAL
IND
PHASE 1
PHASE 2
PHASE 3
APPROVED
SMALL MOLECULE
GENE THERAPY
Clinical Study Information
To participate in a clinical study, a patient must meet certain eligibility criteria, which include certain demographic and disease characteristics that can allow researchers to appropriately evaluate the investigational therapy. If you are considering participating in a clinical study, you should discuss it with your physician. If you have questions about clinical trial eligibility please contact us at TrialRecruitment@Ultragenyx.com.
