Diverse clinical and preclinical pipeline
We are advancing clinical development programs across multiple rare disease therapeutic areas and drug modalities. We also have a broad translational research department with more than 15 different programs and the goal to advance one new program into clinical trials every one to two years.
Clinical Study Information
To participate in a clinical study, a patient must meet certain eligibility criteria, which include certain demographic and disease characteristics that can allow researchers to appropriately evaluate the investigational therapy. If you are considering participating in a clinical study, you should discuss it with your physician. If you have questions about clinical trial eligibility please contact us at TrialRecruitment@Ultragenyx.com.