Our Purpose

Leading the future of rare disease medicine

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Ultragenyx was founded to create a steady pipeline of new and effective therapies for patients with rare and ultra-rare diseases. It is our shared belief that we will achieve this by creating a people-first ethos that puts patient communities and our employees at the center of our approach and mission.

EMIL D. KAKKIS, M.D., Ph.D.
CHIEF EXECUTIVE OFFICER AND PRESIDENT

Grant Programs

We are committed to improving the lives of patients with rare and ultra-rare genetic diseases through educational initiatives, patient advocacy, research, and access to information. Our specific focus is on patient and professional organizations that provide vital support to the rare disease community.

Learn more about our grant programs

Our Ethics

We are committed to maintaining the highest standards of honest and ethical business conduct, and we make this commitment to the patients we treat, our business partners, our customers, our shareholders, our community, the government agencies that regulate our business, and ourselves.

View our Global Code of Conduct