our rare formula

Relentless dedication to serving patients with serious rare and ultra-rare genetic diseases

At Ultragenyx, we have a unique formula for drug development that reflects our shared urgency to accelerate the timelines for delivering safe and effective new medicines to patients. We do this by taking a deliberate approach in three areas:


Our management team is experienced in all aspects of biopharmaceutical development and commercialization.

Meet our executives Meet our board of directors


Our success to date is driven by our productive partnerships with academia and industry.

Learn more about the companies with whom we are collaborating


We are interested in hearing from people who, like us, are focused on improving the lives of people living with serious rare and ultra-rare genetic diseases.

Want to get in touch? Contact us