Presentations & Publications

KRN23 for XLH

KRN23 for TIO

rhGUS for MPS 7

rhPPCA for Galactosialidosis

UX007 for FAOD

UX007 for Glut1 DS


The prior materials, except for those marked with an asterisk*, are prepared by third parties other than or independently from Ultragenyx Pharmaceutical Inc. (“Ultragenyx”) and do not reflect the opinion of Ultragenyx. Additionally, Ultragenyx is not involved in the preparation of these materials, such materials are not under the control of Ultragenyx, and Ultragenyx does not undertake any obligation to update any of the information presented in such materials. The foregoing materials have been made available by Ultragenyx to provide additional information regarding the epidemiology and mechanism of the indications it is studying and the mechanism and preclinical and clinical information related to its product candidates as produced and assessed by outside investigators.­